Found 5 matching trials
Long Term Safety Follow up of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich Syndrome
PHASE1An open follow up study of patients enrolled in the Phase 1/2 clinical tria...
Status
Active Not Recruiting
Location
Hopital Necker - Enfants Malades
A Clinical Study to Evaluate the Use of a Cryopreserved Formulation of OTL-103 in Subjects With Wiskott-Aldrich Syndrome
PHASE3This is an open-label, single arm study to evaluate the cryopreserved formu...
Status
Active Not Recruiting
Location
Children's Healthcare of Atlanta, Inc
Gene Therapy for Wiskott-Aldrich Syndrome (WAS)
PHASE1This is a phase I/II study to evaluate the safety and efficacy of Hematopoi...
Location
Great Ormond Street Hospital
Gene Therapy for WAS
PHASE1This is a phase I/II study to evaluate the safety and efficacy of Hematopoi...
Location
HΓ΄pital Necker-Enfants Malades
Gene Therapy for Wiskott-Aldrich Syndrome
PHASE1This is phase I/II protocol to evaluate the safety and efficacy of WAS gene...
Location
Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET)